Belief Biomed Congratulates Partner Askbio On IND Acceptance By FDA For Investigational Gene Therapy For Late-Onset Pompe Disease

Belief Biomed Congratulates Partner Askbio On IND Acceptance By FDA For Investigational Gene Therapy For Late-Onset Pompe Disease. SHANGHAI, Jan. 14, 2026 /PRNewswire/ -- AskBio Inc. (AskBio), a gene ...
pharmaphorum

FDA removes barriers to cell, gene therapy development

"Regulatory flexibility must be tailored for cell and gene therapies," commented FDA Commissioner Marty Makary. "These are ...
Clinical Trials Arena on MSN

FDA increases manufacturing flexibility for cell and gene therapies

Clinical and commercial quality controls are eased as the FDA looks to expedite therapy approvals in areas of unmet need.

AskBio Announces FDA Acceptance of Investigational New Drug (IND) Application for AB-1009 Gene Therapy for Treatment of Late-Onset Pompe Disease (LOPD)

AB-1009 program advances to Phase 1/Phase 2; clinical trial initiated in the United StatesTherapy granted United States Food ...
DISABLED ENTREPRENEUR UK on MSN

What is cell & gene therapy AI

Cell and gene therapy are revolutionary approaches to treating diseases at the molecular level. They involve the manipulation ...

Genprex Provides Clinical Update on Diabetes Gene Therapy Program

Genprex, Inc. ("Genprex" or the "Company") (NASDAQ: GNPX), a clinical-stage gene therapy company focused on developing ...
FiercePharma

Gene therapy CDMO Artis BioSolutions launches with acquisition of Landmark Bio

Out of the shadows, new CDMO Artis BioSolutions has decloaked on a mission to tackle the tricky production process for advanced therapeutics. Artis officially emerged from stealth on Wednesday, ...

Retired HGV driver undergoes heart bypass using gene therapy to reduce risks

A retired HGV driver was the first person in the world to take part in a clinical trial to extend the lifespan of blood ...
WKRG

Teknova Expands Proprietary AAV-Tek™ Solutions Product Line to Deliver End-to-End Solutions for Gene Therapy Process Development

HOLLISTER, Calif., July 11, 2023 (GLOBE NEWSWIRE) -- Alpha Teknova, Inc. (“Teknova”) (Nasdaq: TKNO), a leading producer of critical reagents for the research, discovery, development, and ...
FiercePharma

Sarepta stands behind Elevidys after FDA requests gene therapy be pulled from market

As the controversy over the safety of Sarepta Therapeutics’ gene therapies comes to a head, the biotech is standing firm behind its approved Duchenne muscular dystrophy (DMD) treatment. The FDA, for ...
Forbes

Health Plans Brace For Cell And Gene Therapy Costs

Forbes contributors publish independent expert analyses and insights. Bruce Japsen writes about healthcare business and policy. More than 70% of employers and health plans expect affordability of gene ...
Reuters

Gene therapy loses luster as investors eye quicker returns from weight-loss drugs

Venture capital investment in gene therapies fell to $1.4 billion in 2024 from 2021 peak of $8.2 billion Total global biopharma venture funding rose to $27 billion in 2024 from $23.2 billion in 2023 ...